500 WARREN CORPORATE CENTER DRIVE, WARREN, NJ
Provides Corporate Update and Reports First Quarter 2026 Financial Results
Annual Report to Security Holders
Appoints Biotech Banking Pioneer Jessica Chutter to Board of Directors
Provides Corporate Update and Reports Fourth Quarter and Full Year 2025 Financial Results
Provides Regulatory Update on Translarna™
Investor Presentation
Amendment to Royalty Purchase Agreement with Royalty Pharma Investments
Provides Corporate Update and Reports Third Quarter 2025 Financial Results
Q1
FY 2024
Q3
Q2
FY 2023
Notice of Exempt Offering of Securities
S-3ASR
Registration Statement for Securities to be Offered to Employees
Prospectus filed pursuant to Rule 424(b)(5)
Definitive Proxy Statement
Additional Proxy Materials
Statement of Changes in Beneficial Ownership
Amended Schedule 13G - Ownership Report
Notice of Proposed Sale of Securities
Submission Upload
Correspondence